Alport Syndrome – Causes, Symptoms and Treatment

Alport Syndrome (AS) is an inherited disorder ofThere may be nerve deafness and congenital eye
the basement membranes of the kidney, eye andabnormalities associated with Alport syndrome.
ear. People who inherit defective genes for theThe cause is a mutation in a gene for collagen.
"collagen" proteins in these basement membranesThe disorder is uncommon, and most often
may develop progressive loss of renal function,affects males since the genetic defect is typically
deafness and abnormalities of the eye. In thefound on the X chromosome.
kidneys, glomerular basement membranesGenes that Cause Renal Failure: Dialysis patients
normally act like filters, allowing fluid to moveand their relatives with diabetes, high blood
from blood vessels to urine while retaining proteinpressure and/or kidney failure are sought for a
and red blood cells within the bloodstream. Thus,study at Case Western Reserve University to
one of the early signs of Alport syndrome mayidentify genes that contribute to or cause renal
be leakage of small amounts of blood or proteinfailure. Family participants will each receive $25 for
into the urine during childhood.Collagen-containingtheir blood sample and complete medical and
membranes are also important for the shape offamily histories.
the lens of the eye and the structure of the innerOther common mutations lead to premature
ear.termination of protein translation and loss of the
Causescarboxy-terminal NC1 domain, resulting in
Alport syndrome is an inherited form of kidneydefective interchain association and formation of
inflammation (nephritis). It's caused by a mutationthe collagen network.
in a gene for a protein in connective tissue, calledSymptoms
collagen. The disorder is uncommon, and mostHearing loss can be present at birth (congenital) or
often affects males. Women can transmit thebecome evident later in life (acquired deafness).
gene for the disorder to their children, even ifThe distinction between acquired and congenital
they have no symptoms.deafness specifies only the time that the
When mutations prevent the formation of typedeafness appears. It does not specify whether
IV collagen fibers, the basement membranes ofthe cause of the deafness is genetic (inherited).
the kidneys are not able to filter waste productsTreatment
from the blood and create urine normally, allowingThere is no cure for Alport’s syndrome, but
blood and protein into the urine. The abnormalitiestreatment is available to ensure the kidneys can
of type IV collagen in kidney basementfunction as fully as possible. This includes limiting
membranes cause gradual scarring of the kidneys,your intake of salts and fluids, high amounts of
eventually leading to kidney failure in many peoplewhich put too much strain on the kidneys. Your
with the disease.doctor will also recommend that you take steps
Approximately 50-80% of patients with X-linkedto control your blood pressure and potassium
Alport syndrome have mutations in the COL4A5levels. If you have nephrotic syndrome, your
gene. Several hundred mutations, includingdoctor will recommend lowering your fluid intake;
missense mutations, splice-site mutations, andtaking medications called diuretics, which help the
small deletions account for most cases of X-linkedkidneys eliminate wastes from the body by
Alport syndrome. Few mutations have been foundincreasing urinatation; and eliminating all salts from
in more than 1 family.your diet. You may also need to receive a
Alport syndrome is a form of hereditary nephritis.transfusion of albumin.